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Fostering continuous quality improvement in a European rare disease network: Where are we now?
Abr 29, 2026
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Orphanet Journal of Rare Diseases
Orphanet Journal of Rare Diseases
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Clinical spectrum, diagnosis, cognitive outcomes and therapeutic strategies in pediatric Rasmussen syndrome: a 10-year cohort from a tertiary pediatric center
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Prevalence of depressive and anxiety symptoms among patients consulting a rare disease outpatient clinic for rare and undiagnosed diseases in China
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