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The withdrawal of beti-cel therapy for β-Thalassemia from the European market: a multistakeholder perspective
Sep 4, 2026
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Orphanet Journal of Rare Diseases
Orphanet Journal of Rare Diseases
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Advancing continuous glucose monitoring for children and young people with hyperinsulinism – a white paper from the Congenital Hyperinsulinism International Collaborative Research Network
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